Developing a Potency Assays Strategy for a Novel Human Bocavirusbased Gene Therapy

Time: 5:00 pm
day: Day 2


  • What is human bocavirus and why is it is suitable vector for gene therapies against Cystic Fibrosis?
  • Utilising an Ussing chamber chloride ion current as a novel functional assay to assess potency
  • Reflecting on the lessons and learnings from using a novel vector approach to overcome developmental hurdles upfront